Oregon Health & Science University is opening a new Center for Embryonic Cell and Gene Therapy to study experimental treatments for Parkinson's disease, multiple sclerosis and a range of other conditions caused by diseased or injured cells in the human body.
A busy Servier wants to explore Celladon's technology to see if there are some small molecule applications to diabetes and other metabolic conditions that warrant clinical development.
An experimental gene therapy developed by investigators at the Icahn School of Medicine at Mount Sinai successfully regenerated heart muscle in pigs following a heart attack.
Third Rock Ventures has cut the ribbon on its latest startup, pledging $45 million to launch Cambridge, MA's Voyager Therapeutics, a gene therapy biotech with a promising platform for central nervous system treatments.
An experimental gene therapy has restored eyesight to 6 patients in a small Phase I clinical trial in the U.K., exceeding expectations of investigators, according to a new study in The Lancet.
In what could become a vast improvement to the delivery of gene therapy within the body, U.S. researchers have developed injectable DNA-carrying viruses that could eventually stop tumor growth or make chemotherapy more effective.
Researchers at the Icahn School of Medicine at Mount Sinai Hospital used a virus to deliver genes directly to the heart to reverse heart failure, shrinking an enlarged heart and improving its function.
2012 Fierce 15 member Celladon has boosted its IPO goals, seeking as much as $92 million to help get its gene therapy for heart failure through a Phase IIb study and into Phase III.
Fidelity Biosciences is placing a big bet on gene therapy, funding the launch of startup Dimension Therapeutics with some licensed patents and a plan to develop novel treatments for hemophilia.
Combining gene therapy plus an infusion of stem cells helps heal wounds faster in mice, a discovery that could eventually lead to better treatments for older people with wounds, who fail to heal as well as younger patients.