Genomics News

New animal research into PTC124 at the University of Massachusetts Medical School indicated that it is effective in correcting the genetic disorder that causes Duchenne muscular dystrophy in about 15 percent of cases. Researchers say that DMD is sometimes triggered when the assembly process required to make proteins necessary for good health is interfered with by a DNA "nonsense mutation." The therapy works by prompting cells to ignore the mutations. The therapy, which is being developed …